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WATCH: Santhera Update to the Duchenne Community – Webinar Recording

On May 8, 2019, Santhera joined Parent Project Muscular Dystrophy for a webinar to provide the community with an update about respiratory health in Duchenne muscular dystrophy and the ongoing SIDEROS clinical trial. If you…

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Your Duchenne Registry Data: Researchers Analyze Steroid Use

We have exciting news to share from The Duchenne Registry. A study using the Registry data was published this week in a well-known international journal, BMC Neurology. This study was led by researchers at Catabasis…

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PPMD’s 2019 Annual Conference Agenda is Now Available!

PPMD is excited to unveil the agenda for our 2019 Annual Conference in Orlando, Florida, June 26 – June 30, 2019! Each year, PPMD works hard to put together a comprehensive agenda featuring updates in…

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End Duchenne Tour Recap: Portland, ME

PPMD had the opportunity to travel to Portland, ME on April 27 for our third End Duchenne Tour stop of 2019. We were joined by 14 local families, 11 of our industry partners, and 3…

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Newborn Screening Saves Lives Reauthorization Act Introduced in House of Representatives

Yesterday, the Newborn Screening Saves Lives Reauthorization Act was introduced in the House of Representatives. PPMD is extremely proud to be a leading coalition voice in this milestone legislation aimed at eliminating preventable newborn deaths…

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WATCH: Capricor’s Clinical Program – Webinar Recording

On Wednesday, April 24, 2019, Capricor joined Parent Project Muscular Dystrophy for a webinar to update the community on Capricor’s HOPE2 clinical program. If you missed the live event, the recording can be found below….

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PPMD Announces Univ. of Utah Health & Intermountain Primary Children’s as 25th Certified Duchenne Care Center

Today Parent Project Muscular Dystrophy (PPMD) named University of Utah Health (U of U Health) and the Intermountain Primary Children’s Hospital in Salt Lake City, Utah the 25th Certified Duchenne Care Center (CDCC). This expanding…

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The Early Bird Rate for PPMD’s 2019 Annual Conference Ends Wednesday!

PPMD’S 2019 ANNUAL CONFERENCE JUNE 26 – JUNE 30, 2019 ORLANDO, FL Your last opportunity to join us at the 2019 PPMD Annual Conference at our Early Bird Registration Rate ends Wednesday, April 24! This…

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PPMD Awards $100,000 Grant to Nationwide Children’s Hospital to Further Explore GALGT2 Gene Therapy

PPMD is excited to announce that Drs. Paul Martin and Kevin Flanigan from the Research Institute at Nationwide Children’s Hospital have completed work under a $100,000 grant exploring GALGT2 gene therapy technology as a potential treatment…

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Wave Life Sciences Announces Suvodirsen Phase 1 Safety and Tolerability Data and Phase 2/3 Clinical Trial Design

Wave Life Sciences shared safety and tolerability data from their Phase 1 clinical trial evaluating investigational suvodirsen (WVE-210201) in patients with Duchenne. The results from this trial support progressing to a Phase 2/3 clinical trial,…

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