Blog

PPMD Awards $175,000 Grant to UCLA to Explore Optimization of CRISPR Technology in Duchenne

Parent Project Muscular Dystrophy (PPMD) is excited to announce that Drs. Melissa Spencer and April Pyle from the David Geffen School of Medicine at UCLA and the Center for Duchenne Muscular Dystrophy at University of…

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PPMD Contributes to National Report on Caregiver Roles in Medical Product Development

For the last few years, PPMD has been working in partnership with the National Alliance for Caregiving, which has included the participation of PPMD’s Annie Kennedy on the planning committee of a national summit that…

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WATCH: Domagrozumab as a Potential Treatment for Duchenne – Webinar Recording

On May 22, 2019, Pfizer Inc. joined Parent Project Muscular Dystrophy for a webinar to provide the community with an overview of the primary safety and efficacy results from the Phase 2 clinical trial. Additional…

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Jerry Mendell, MD named inaugural recipient of the Allen Distinguished Scholar in Pediatric Research

Nationwide Children’s Hospital has announced the inaugural recipient of the Allen Distinguished Scholar in Pediatric Research, Jerry Mendell, MD. Congratulations to Dr. Mendell on this incredibly deserved recognition! Thank you for your ongoing work in…

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PPMD’s Certified Duchenne Care Center Program – 2018 Impact & Progress

For 25 years, care has been at the heart of everything PPMD does. We strive to ensure that people living with Duchenne are living longer, stronger lives, by helping you access expert healthcare providers, a…

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PPMD Signs on to Defense Health Research Letters

PPMD is proud to serve as a member of the Defense Health Research Consortium. Last week, letters were sent to both houses of Congress asking for their continued support for the critical and highly successful…

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Race Athlete Spotlight: Alison Joseph

When Alison Joseph’s two sons were diagnosed with Duchenne, she immediately felt moved to do something to help raise money and awareness. Alison, along with her husband William Small and 44 of their family members…

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PPMD Hosts Duchenne Clinical Outcomes Workshop

PPMD has been working for many years to engage critical policy makers and stakeholders within the regulatory and access environments. While we have learned a great deal over the past two years as we have…

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PPMD Awards $100,000 Grant to UCLA to Map the Immune Phenotype in Duchenne Muscular Dystrophy

PPMD is excited to announce that Dr. Carrie Miceli from the Center for Duchenne Muscular Dystrophy at University of California – Los Angeles (UCLA) is the recipient of a $100,000 grant to continue her work to…

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Solid Biosciences Provides Update on IGNITE DMD Status and New Clinical Sites

Solid Biosciences shared an update on the progress of their IGNITE DMD Phase I/II clinical trial for investigational microdystrophin gene transfer, SGT-001. The update includes news about initiating dosing for their higher dose cohort of…

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