February 3, 2020

PTC Announces Publication of Data Showing Translarna Significantly Preserves Ability to Walk for Longer

PPMD is excited to learn that PTC Therapeutics announced real-world data showing that boys with nonsense mutation Duchenne treated with Translarna™ (ataluren) and standard of care, preserved the ability to walk for years longer than…

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January 23, 2020

End Duchenne Tour Connect Group Session: Houston, TX

PPMD’s End Duchenne Tour made a stop in Houston, TX on Saturday, January 18. We were joined by over 40 people, including PPMD’s Connect Coordinators for South Texas, several PPMD families, and some of the…

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January 21, 2020

Santhera Shares Winter 2020 Community Update

Santhera Pharmaceuticals shared a letter with the community, emphasizing that their main focus in the U.S. right now is to bring the SIDEROS clinical trial to full enrollment. Learn more about this clinical trial, including…

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January 15, 2020

WATCH: Update on Investigational Suvodirsen in Duchenne Muscular Dystrophy – Webinar Recording

On December 20, 2019, Parent Project Muscular Dystrophy (PPMD) and World Duchenne Organization (WDO) hosted an informational webinar with the Wave Life Sciences team to discuss their decision to discontinue development of suvodirsen for patients…

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January 15, 2020

PPMD’s Duchenne Drug Development Roundtable Creates Clinical Trial Harmonization Guidances

PPMD is excited to share the recently developed Clinical Trial Harmonization Guidances. These guidances are the result of PPMD’s Duchenne Drug Development Roundtable working collaboratively in the pre-competitive space to encourage better consistency across companies…

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January 8, 2020

Italfarmaco Shares Winter 2020 Newsletter

Italfarmaco has shared the Winter 2020 issue of their newsletter, including updates on the Givinostat Development Program. Click here to download.

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January 8, 2020

Catabasis Shares January 2020 Newsletter

Catabasis shares the latest edition of their community newsletter, including information about the Phase 3 PolarisDMD trial enrolling the expected patient population and a partnership with our friends at Duchenne UK to evaluate edasalonexent in…

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January 7, 2020

PPMD’s Endurance Program – Race to End Duchenne – Celebrates 15 Years of Going the Distance to End Duchenne

Parent Project Muscular Dystrophy (PPMD) celebrates the 15th anniversary of our endurance fundraising program, Race to End Duchenne, this weekend in Orlando. Over 170 team members will participate in the 2020 WALT DISNEY WORLD® MARATHON…

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January 3, 2020

Thank you for making today better!

We can’t begin to express our gratitude to everyone who donated to PPMD this holiday season! Thanks to your generosity, and a community match, I am thrilled to announce that we reached our ambitious fundraising…

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December 27, 2019

Donate to PPMD today and help make tomorrow TWICE as strong

I know we are right in the thick of the holiday season with a new year quickly approaching, so I thank you for taking a minute to read this note. The holidays can be a…

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