November 17, 2020

ReveraGen Receives $3.3 Million NIH Grant for NDA Preparations for Vamorolone in Duchenne

The National Institute of Neurological Disorders and Stroke (NINDS) of the National Institutes of Health (NIH) has awarded a $3.3 million grant to ReveraGen Inc. to support the advancement of vamorolone towards FDA submission and…

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November 16, 2020

Duchenne UK, MDA & PPMD Award $686,500 Grant To Develop Easier Way To Measure if New Treatments Are Working

In an unprecedented collaboration designed to speed research advances, Duchenne UK, the Muscular Dystrophy Association (MDA), and Parent Project Muscular Dystrophy (PPMD) have announced a joint grant of $686,500 to Dr. William Evans (principal investigator)…

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November 13, 2020

Get Ready to Tackle Duchenne! Coach To Cure MD is this Weekend!

We are just days away from the 13th Annual Coach To Cure MD presented by Werner Ladder on Saturday, November 14! This weekend, AFCA Coaches around the country will be wearing Coach To Cure MD patches,…

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November 10, 2020

PPMD’s Ground-Breaking Effort: An Update After One Year of Our Newborn Screening Pilot for Duchenne

14,000 Babies Tested in Partnership with New York State and NBSTRN; Data Presented at Association of Public Health Laboratories Newborn Screening Virtual Symposium Parent Project Muscular Dystrophy (PPMD) today announced that our Newborn Screening Pilot…

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November 9, 2020

Exciting news! Country star Chase Rice joins Coach To Cure MD!

Fall is here and college football is in full swing…which means it is time to huddle up for the 13th Annual Coach To Cure MD, presented by Werner Ladder on Saturday, November 14! As we all…

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November 6, 2020

Sarepta to Commence Dosing of Next Study with Commercial Process Material for SRP-9001 Gene Therapy

We are encouraged by the result of Sarepta’s Type C meeting with the FDA. Type C meetings are a “catch all” category and include any topics concerning the development and review of a product. This…

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November 5, 2020

End Duchenne Tour 2020: Virtual Tour Stop in St. Louis, MO

End Duchenne Tour 2020: Virtual Tour Stop in St. Louis, MO On Saturday, October 17, we spent the morning with the Duchenne community in St. Louis, MO and the surrounding region for another End Duchenne…

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November 4, 2020

Connect with the Experts: Key Takeaways from PPMD’s Endocrine Series

In case you missed it, over the past three weeks PPMD’s SVP of Clinical Care, Rachel Schrader was joined by Duchenne endocrine experts and members of the PPMD Adult Advisory Committee (PAAC) to discuss important…

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November 4, 2020

WATCH: Connect with the Experts – Height and Weight (Endocrine Series)

The body’s endocrine system is made up of glands that produce hormones, which are chemical messengers. Examples are growth hormone (that tells your body when to start and stop growing) and testosterone (the male hormone…

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November 3, 2020

PPMD Urges Congress To Make It Easier for Providers To Treat Children From Other State Medicaid Programs

PPMD joined 22 prominent Organizations and Institutions in a letter urging Congress to enact the Accelerating Kids’ Access to Care Act (H.R. 5900 and S. 4717) by the end of the current Congress. This bipartisan…

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