Blog

Exciting News! Your gift will be Matched Dollar-for-Dollar up to $50,000

There is nothing ordinary about Duchenne. We all know that. Our Duchenne story started in the ER. At two years old, my middle son was involved in a serious accident and went into cardiac arrest….

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WATCH: Gene Therapy – Turning Obstacles into Possibilities (Webinar Recording)

On April 20, 2021, PPMD’s Pat Furlong & Eric Camino were joined by Drs. Nagaraju and Shieh for an interactive panel discussion on the lessons learned in Gene Therapy, current challenges for our community, and…

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PPMD’s End Duchenne Tour turns 5!

In late 2015, we had a discussion at the PPMD office in Hackensack. Was it time to kick our local educational events up a notch? Have we certified enough centers to have a “home base”…

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Join us Tuesday, April 20 for a conversation about PPMD’s Gene Therapy Initiative

Turning obstacles into possibilities is what initially lead me to joining PPMD. I had little personal experience with our Duchenne community before I began working with Dr. Jerry Mendell and a number of other fantastic…

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Johnson & Johnson COVID-19 Vaccine Pause: What Does This Mean for the Duchenne Community?

Yesterday, April 13, 2021, the CDC and FDA issued a joint statement addressing the recently approved Johnson & Johnson (Janssen) (J&J) COVID-19 vaccine, recommending a pause in administration of doses. This pause is the result…

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Females with Dystrophinopathy: Publication of PPMD’s Pre-Conference Meeting Summary & Recommendations

Much has been explored about males living with Duchenne, but what about the many females who are living with symptoms (i.e., skeletal muscle weakness, cognitive issues and/or cardiomyopathy) of this diagnosis? In June of 2019,…

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Take Action Before House Letter Closes! Deadline is Friday, April 16

Our numbers in the House of Representatives for this year’s Funding Request to Congress continue to rise! We have 65 House members signed on so far with the deadline for signatures this Friday, April 16….

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Support PPMD to turn obstacles into possibilities

When I think about Duchenne research, I am awestruck. It is hard to wrap my head around how far we’ve come since my boys were diagnosed, but I also know we still have quite a…

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PPMD Awards $31,500 Grant to Understand Immune Response to CRISPR/Cas-9 Gene Editing Strategies

PPMD is excited to award the University of Missouri School of Medicine a bridge grant for $31,500 to continue evaluating CRISPR therapy in a pre-clinical model of Duchenne. The project is led by Dongsheng Duan,…

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Crafting to End Duchenne

Crafting to End Duchenne Restrictions on large gatherings made the Labbadia family’s annual kickball tournament fundraiser impossible in 2020, so instead they chose an activity they could do together as a family while bringing holiday…

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