Blog

2022 End Duchenne Tour Recap: Atlanta, GA

2022 End Duchenne Tour Recap: Atlanta, GA The PPMD team was excited to travel to Atlanta for our first in-person End Duchenne Tour stop since 2020. More than 30 people came together to hear about…

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Win a NEW Xbox Series X with PPMD’s Duchenne Registry!

Win a NEW Xbox Series X! For all of you gamers and parents of gamers, PPMD’s Duchenne Registry is excited to announce we will be giving away a brand new Xbox Series X to one…

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Nationwide Children’s Announces Restoration of Full-Length Dystrophin Using Dup 2 Gene Therapy Approach

PPMD is very excited to see promising results shared from Nationwide Children’s scAAV9.U7.ACCA gene therapy trial, a Phase 1/2 study aiming to induce exon skipping for individuals with a duplication of exon 2 to restore full-length…

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WATCH: PPMD & Pfizer Discuss Updates on CIFFERO Phase 3 Gene Therapy Trial

Recently Pat Furlong, PPMD’s founder and CEO, sat down with Dr. Beth Belluscio, Pfizer’s Global Clinical Lead of Rare Neurological Disorders, to discuss Pfizer’s learnings from previous gene therapy studies and updates on the CIFFERO…

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Entrada Therapeutics Shares New Data on ENTR-601-44 Exon Skipping Therapy

Entrada Therapeutics has shared new data from a preclinical study evaluating ENTR-601-44, an exon-skipping therapy set to target individuals with Duchenne amenable to exon 44 skipping. We are pleased to hear new data on this…

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Sign up today! Virtual Race Series-Power of Us

Sign up today for the Race to End Duchenne Virtual Race Series-May 21, 2022 – June 19, 2022! The Power of Us is stronger than any one of us alone. Join us for the Race…

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PPMD Announces 30th Certified Duchenne Care Center at Helen DeVos Children’s Hospital

Today Parent Project Muscular Dystrophy announced the expansion of our renowned Certified Duchenne Care Center (CDCC) Program with pediatric CDCC certification of the clinic at Spectrum Health Helen DeVos Children’s Hospital (HDVCH) in Grand Rapids,…

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Race Athlete Spotlight: Catalina Rodriguez

Catalina Rodriguez joined the Race to End Duchenne team and ran the runDisney Princess 5K in February of 2022. With the support of her son and daughter, she finished with pride. Meet Catalina Why did…

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Regenxbio Announces Delay in Timeline for Initiation of First Participant Dosed in Affinity Duchenne Trial

REGENXBIO today announced that it will delay the initiation of dosing in the Phase I/II AFFINITY DUCHENNETM trial studying RGX-202 in participants with Duchenne, due to an unexpected observation in the final stages of manufacturing…

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PPMD Brings Caregivers Together to Kick off The Power of Us Summit Series

PPMD Brings Caregivers Together to Kick off The Power of Us Summit Series Today PPMD is excited to convene the first meeting in The Power of Us Summit Series, our series of mental wellness retreats…

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