January 5, 2023

Thank You for Helping Ensure Hearts Grow Stronger With Every Beat!

I am grateful for your generosity this year and excited to announce that we have surpassed our goal to provide support to PPMD’s Cardiac Initiative and commitment to ACTION, the Advanced Cardiac Therapies Improving Outcomes…

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January 3, 2023

Race Athlete Spotlight: Tammy Cate

With the 2023 Walt Disney World Marathon® Weekend presented by State Farm coming up this week, we’re featuring Tammy Cate who has been a member of the Race to End Duchenne team for over 10…

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December 30, 2022

PPMD Submits Written Comments Following CBER Meeting on Patient Perspectives on Gene Therapy Products

PPMD recently submitted written comments to the Center For Biologics Evaluation and Research (CBER) following Chief Advocacy Officer Ryan Fischer’s participation in the November 15th FDA CBER OTAT Patient-Focused Drug Development Listening Meeting: Patient Perspectives…

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December 27, 2022

Double Your Gift Today.

Being a twin brings with it a unique closeness that few are lucky enough to experience. Having a sibling with Duchenne adds an additional layer to the relationship that is unique as well. I love…

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December 21, 2022

WATCH: Protect Your Lungs This Winter (Webinar Recording)

Connect With the Experts – Pulmonary Management in Winter Season As we embark into the winter season, it’s imperative that individuals with Duchenne and Becker muscular dystrophy are prepared to manage their pulmonary health and…

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December 21, 2022

Help Hearts Grow Stronger and have your gift MATCHED through 12/31!

My son Logan is 10 years old. He is sharp, bright and curious, and it’s amazing to me to watch his brain at work. He has never once let Duchenne slow him down mentally, however…

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December 20, 2022

Entrada Therapeutics Announces Clinical Hold on IND Application for ENTR-601-44 in Duchenne

Entrada Therapeutics has shared that the FDA issued a clinical hold on the Investigational New Drug (IND) application for its ENTR-601-44 program, an exon-skipping therapy set to target individuals with Duchenne amenable to exon 44…

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December 19, 2022

WATCH: A Conversation with PTC Therapeutics (Webinar Recording)

WATCH: A Conversation with PTC Therapeutics (Webinar Recording) PTC Therapeutics recently joined PPMD for a community webinar on Friday, December 9, 2022 for a discussion regarding PTC’s history with the community and plans for the…

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December 15, 2022

Give Today to help my Heart Grow Stronger

I was diagnosed with Duchenne muscular dystrophy at three years old. It was the late 90’s and PPMD was just beginning to grow as an organization. We found Pat Furlong and through her were connected…

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December 14, 2022

Back in Washington, DC! PPMD’s Advocacy Conference Returns March 5-7

Want to be part of history? Want to contribute to future progress in understanding, diagnosing, and treating Duchenne? Register today to join PPMD’s 2023 Advocacy Conference, March 5-7th, in Washington, DC! We are excited to announce…

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