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Race Athlete Spotlight: Tammy Kennedy

Tammy Kennedy has been an avid supporter of the Race to End Duchenne Virtual Series over the past year. Join her in the 79 Mile Challenge starting today! Meet Tammy Why did you choose to…

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PPMD Joins Duchenne Parent Project aps Endocrine & Osteoporosis International Professional Care Meeting

How do we prevent the first fracture? How does weight & puberty affect bone health? How do we understand and implement new therapies? All of these questions and more will be covered this week as…

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Pfizer Completes Enrollment of CIFFERO Phase 3 and DAYLIGHT Phase 2 Gene Therapy Trials

Pfizer announced today that enrollment is now complete for both the Phase 3 CIFFERO study and Phase 2 DAYLIGHT study of PF-06939926 (fordadistrogene movaparvovec) in Duchenne. As always, we are so grateful to all of…

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WATCH: Dyne Therapeutics — Advancing FORCE in the Pursuit of Therapies (Webinar Recording)

Dyne Therapeutics joined PPMD for a community webinar on April 12, 2023 to discuss Dyne’s FORCE™ platform. Ashish Dugar, PhD, MBA, Dyne’s Chief Medical Affairs Officer, and Molly White, Dyne’s Vice President, Global Head of…

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How to Submit Written Testimony for the SRP-9001 FDA Advisory Committee Meeting – Deadline May 5th

Sarepta recently announced that the FDA Advisory Committee meeting for SRP-9001 (delandistrogene moxeparvovec), Sarepta’s investigational gene therapy for Duchenne muscular dystrophy, will be held on May 12th. The event will be completely virtual and a…

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PPMD’s Certified Duchenne Care Center Program – 2022 Impact & Progress

Every single person living with Duchenne deserves the best care possible. It is important that families know who is in charge of delivering the care they need and understand what centers are providing optimal, standardized…

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PPMD’s Knight Hacks is LIVE! Explore Everyday Tips & Tricks for Families

Have you been in search of an easier way to brush your teeth? A new way to organize your snack shelf that makes food easier to access? Great, accessible travel tips? Introducing Knight Hacks: Everyday…

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WATCH: Connect With the Experts – Bone Health in Duchenne (Webinar Recording)

Connect With the Experts – Bone Health in Duchenne PPMD recently hosted a webinar led by expert endocrinologists Dr. Leanne Ward (University of Ottawa), Dr. Janet Crane (Johns Hopkins) and Nadia Merchant (Children’s National) to…

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NS Pharma Announces FDA Clearance of IND for Clinical Trial of NS-089/NCNP-02 Exon 44 Skipping Candidate

PPMD is excited to share that NS Pharma has announced that they have received clearance from the FDA on their Investigational New Drug (IND) application for NS-089/NCNP-02, a potential exon skipping therapy targeting people with…

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Sign up today! Virtual Race Series-79 Mile Challenge

Sign up today for the Race to End Duchenne Virtual Race Series-May 1, 2023 – June 12, 2023! The Virtual Series is back! Join us as we race across the country by completing actions in…

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