September 19, 2023

RSV, COVID, and Flu – oh my!

As school has started and the winter season approaches, the increase in respiratory viruses is soon to come. This year it’s important to protect yourself, your children and your family from all respiratory viruses, but…

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September 15, 2023

PTC Therapeutics Announces Negative European Medicines Agency Opinion Regarding Full Authorization of Translarna

PTC Therapeutics today shared that the Committee for Medicinal Products for Human Use (CHMP) of the European Medicines Agency (EMA) has recommended not renewing the Marketing Authorization for Translarna™ (ataluren), a treatment for Duchenne patients…

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September 13, 2023

Game Day Tips for Coach to Cure MD 2023

The 16th Annual Coach to Cure MD Game Day is Saturday, September 30th! With over 280 schools participating this year, we couldn’t be more grateful to have you on our team! There will be plenty…

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September 11, 2023

Duchenne Action Month: Ways to get involved with PPMD

We know that no one person, company, or organization will end Duchenne. That’s why we are grateful to all of our collaborators – individuals, organizations, and industry partners – who, by joining forces with PPMD,…

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August 31, 2023

CDCC Spotlight: Arkansas Children’s Hospital

Reaching Rural Areas When thinking of expert Duchenne care and research, one may think it only exists in large cities. However, Dr. Aravindhan Veerapandiyan, aka Dr. Panda, the Director of Arkansas Children’s Certified Duchenne Care…

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August 30, 2023

FibroGen Announces Topline Data from Phase 3 LELANTOS-2 Study

FibroGen has announced topline results of the Phase 3 LELANTOS-2 trial of pamrevlumab, their investigational anti-fibrotic monoclonal antibody, for ambulatory patients with Duchenne muscular dystrophy.  Although generally safe and well tolerated, pamrevlumab did not meet…

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August 29, 2023

Breaking barriers together, this Duchenne Action Month and every day

On September 7, we will once again join forces with Duchenne and Becker organizations, families, partners, and all those like minded individuals around the globe to commemorate World Duchenne Awareness Day. This year we acknowledge…

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August 25, 2023

WATCH: Advocating for Access: Navigating Approved Therapies in Duchenne (Webinar Recording)

Understanding and navigating insurance access can be daunting. That’s why PPMD kicked off a new webinar series, “Advocating for Access,” earlier this week with its first monthly installment on Navigating Approved Therapies in Duchenne. PPMD’s…

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August 22, 2023

PPMD Awards $65,000 to Vanderbilt University Medical Center to Advance Understanding of Duchenne Cardiomyopathy

PPMD is excited to award Dr. Jonathan Soslow (Vanderbilt University Medical Center), and his collaborators Drs. Larry Markham (Riley Children’s Hospital) and Christopher Spurney (Children’s National Medical Center), a $65,000 grant to characterize microRNA and…

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August 21, 2023

Safe & Unsafe Medications in Duchenne

PPMD’s Safe & Unsafe Medications Resource lists medications that are frequently used in the management of Duchenne, as well as both over-the-counter and prescription medications used for other conditions not specific to Duchenne that you…

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