Blog

Solid Biosciences Announces FDA Removes Clinical Hold on SGT-001

PPMD is excited to learn that Solid Biosciences Inc. announced that the FDA has lifted the clinical hold on IGNITE DMD, the Company’s Phase I/II clinical trial for its investigational microdystrophin gene transfer, SGT-001. In…

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Jumping Jack Events to End Duchenne Turns 15

For 15 years, the Knight family of Westminster, Colorado has been supporting PPMD’s mission by hosting their annual Jumping Jack Events every June for 15 years now! Named after their son, 17-year—old Jack Knight, Jumping Jack Events started as…

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3rd Annual Kindness Over Muscular Dystrophy Raises $140,000

On June 9, the Curran Family had over 500 attendees and raised over $140,000 at their 3rd Annual Kindness Over Muscular Dystrophy event to benefit PPMD in honor of their son, Conner. The event took…

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A Game Night to End Duchenne

Game Night to End Duchenne in honor of Henry was a huge success last weekend! Raising close to $50,000 with no overhead costs, it was a night filled with close friends of the family and…

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End Duchenne Tour Recap: Birmingham, AL

PPMD was very happy to have the opportunity to meet the team from Children’s Hospital of Alabama and all of the families that came out to our End Duchenne Tour stop on June 6 in the…

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Sarepta Shares Quarterly Update, Including US Clinical Trial Updates

Sarepta has provided another quarterly update to the community, including information on their PPMO (Peptide Conjugated Phosphorodiamidate Morpholino Oligomer), an exon skipping technology designed to efficiently get inside cells, with the goal of producing more dystrophin in…

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Join the Race to End Duchenne

We are thrilled to announce the launch of the new name and look for our endurance program, Race to End Duchenne. This new name reflects the dynamic nature this program has taken on over the…

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Race Athlete Spotlight: Catie Sims

Catie Sims met Garrett Sapp and his family several years ago when she decided to turn her love of running into a way to help others. Since then she has become part of the Sapp…

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WATCH: Introducing PPMO – Webinar Recording with Sarepta Therapeutics

Sarepta Therapeutics, Inc. recently joined Parent Project Muscular Dystrophy (PPMD) for a community webinar update to discuss PPMO, Sarepta’s next generation precision RNA-targeting therapeutic platform for use in Duchenne muscular dystrophy. During the webinar, Sarepta…

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Race Recap: 2018 Walt Disney World Marathon Weekend

We’ve just returned from the Walt Disney World Marathon Weekend, which is where the Run For Our Sons program started, and wow what a weekend it was! From Sean Crosby’s inspirational talk at our Team…

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