September 6, 2018

Updated Duchenne Care Guide for Families

You have probably heard a lot about ‘Care Considerations’. These were the first Standards of Care published in 2010. The purpose of developing Standards of Care is to ensure every person living with the diagnosis…

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September 5, 2018

PPMD Designates American Family Children’s Hospital a Certified Duchenne Care Center

Today Parent Project Muscular Dystrophy (PPMD) named American Family Children’s Hospital in Madison, Wisconsin our 19th Certified Duchenne Care Center. PPMD’s Certified Duchenne Care Center Program, which supports standardized, comprehensive care and services for all people…

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August 30, 2018

Gene Repair Technology Restores Dystrophin Expression in Canine Model of Duchenne

We are encouraged to learn that Exonics Therapeutics, Inc., a biotechnology company focused on developing gene editing therapies to treat patients with Duchenne and other neuromuscular diseases, today announced the publication of a preclinical study…

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August 30, 2018

Pfizer Terminates Domagrozumab (PF-06252616) Clinical Studies for the Treatment of Duchenne

We are deeply disappointed to learn that Pfizer is terminating two ongoing clinical studies evaluating domagrozumab (PF-06252616) for the treatment of Duchenne: a Phase 2 safety and efficacy study (B5161002) and an open-label extension study…

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August 29, 2018

One Month Till Game Day!

It’s the start of the football season and we want YOU to help your local team celebrate this year’s 11th Annual Coach To Cure MD! There’s still plenty of time for you to put together…

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August 23, 2018

Overview: Access to Unapproved Investigational Drugs in the U.S.

Overview: Access to Unapproved Investigational Drugs in the U.S.* Like you, PPMD has had many questions about the way we can access UNAPPROVED investigational therapies in Duchenne. Expanded access, compassionate use, Right to Try –…

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August 22, 2018

Go Casual for World Duchenne Awareness Day!

This year, celebrate World Duchenne Awareness Day on September 7 by hosting a Jeans Day at your school, group or office! Raise even more funds by getting your employer to match all donations that come in. You…

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August 22, 2018

ReveraGen Announces First Patient Enrollment in International Pivotal Trial of Vamorolone in Duchenne

  ReveraGen BioPharma announced the initiation and first patient enrollment in a double-blind, placebo- and prednisone-controlled clinical trial (VBP15-004) of vamorolone, a first-in-class dissociative steroidal anti-inflammatory, in Duchenne. This VISION-DMD study will enroll approximately 120…

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August 20, 2018

PPMD’s Certified Duchenne Care Center Program – August 2018 Bi-Annual Report

PPMD’s Certified Duchenne Care Center (CDCC) Program was developed to make comprehensive Duchenne care and services, provided in agreement with the CDC Care Considerations, available and accessible to as many families as possible, and to strengthen…

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August 16, 2018

Mitchell’s Run Thru Rockford Turns 20

For 20 years, residents of Rockford, Michigan have been supporting PPMD’s mission to end Duchenne by participating in Mitchell’s Run Thru Rockford. Created and organized by the Peterson family, in honor of their 22-year-old son Mitchell,…

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