As a family living with Duchenne, time is everything to us. Decades of trials and research have paved the way for a new era, ushering in a reality with a growing landscape of both approved and investigational therapies. As a community, we have an opportunity to move the science not only further, but faster by supporting PPMD’s Dystrophinopathy Clinical Research Network (DCRN).

Now is the time to leverage innovative adaptive trial designs. Now is the time to incorporate novel data sharing methodologies to accelerate the pace of research and discovery from decades to years.

PPMD’s Dystrophinopathy Clinical Research Network (DCRN) will transform Duchenne and Becker care by comprehensively collecting and analyzing patient data across diverse therapeutic experiences and fostering provider collaboration through innovative technology to drive improved patient outcomes.

This is new research for a new reality. And now, the timing is right for your donation to go twice as far.

My son Jaylen has participated in three clinical trials since the age of five. He was also an early recipient of gene therapy. We are extremely grateful that Jaylen has had these opportunities and realize that many others have not. PPMD’s DCRN aims to accelerate the pace of discovery from decades to years – so that more families can have opportunities and access to transformative therapies. Your gift today plays an integral role in the development of the DCRN and its impact on this generation of individuals Duchenne and Becker.

I am tremendously grateful to this community and the decades of hard work that have led us to today. I am proud of Jaylen and others like him for the sacrifices they’ve made to important research. While we’ve achieved remarkable milestones, significant challenges remain in deepening our understanding of Duchenne and Becker as well as in understanding how different therapies can work together to truly change our outcomes.

We are at a pivotal moment in the fight to end Duchenne. It is my hope that we can accelerate progress and give Jaylen and all people living with Duchenne and Becker the chance to spend more time doing what they love.

DOUBLE your gift today. Together, let’s move the science further, faster.

Thank you,

Limca Jhaveri
Duchenne Parent and PPMD Connect Coordinator

P.S. Your gift goes twice as far now through 12/31. Join us in advancing the research evolution with a donation today.