As we prepare for the ball to drop and the confetti to fall, I am struck by the significance that this will be PPMD’s 30th year, and find myself reflecting on the remarkable milestones achieved in our community. These victories continually fill me with hope for the future. The dedication of this community drives us forward and ignites our momentum, just as it has over the past three decades.

As the New Year draws closer, I ask you to join me in securing a future where gene therapy can become a reality for all who need it. Have your gift DOUBLED before time runs out!

In 2017, PPMD launched our Gene Therapy Initiative and we’ve since invested over $7 million in gene therapy approaches and identified challenges and opportunities for advancement within the field. Together, we’ve reached an extraordinary milestone: the accelerated approval of the first gene therapy for Duchenne. Our foundation is strong, but our work is not done. Give by midnight and your gift to support PPMD’s Gene Therapy Initiative will go twice as far.

Help PPMD raise $500,000 by midnight tonight. All gifts matched!

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Your generosity will help us deepen our understanding of the long-term effects of this treatment on the heart, prioritize research for next-generation and future-generation gene therapies and combination therapies, work to ensure pre-existing antibodies are not a barrier to otherwise eligible individuals, and accelerate the path to repeat dosing.

Today is the last day to help us meet our $500,000 goal to fund PPMD’s Gene Therapy Initiative.

This work is deeply personal to me. Your unwavering support empowers us to do something today that I couldn’t do for my sons so many years ago. As we begin a year of recognition, PPMD’s 30th anniversary in 2024, I’m incredibly proud that our work as a community has transformed gene therapy from a once-distant hope into a tangible reality today for many living with Duchenne.

Help us fight for every future.

As I pour my glass of champagne at midnight, I will toast to YOU. The progress we’ve made over the last 30 years would not have been possible without your unwavering dedication to our cause.

I am eternally grateful to each of you. Now and always.

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Sincerely,

Pat Furlong
Founding President & CEO

P.S. Double your impact before the end of 2023. Make your tax-deductible gift by midnight and your gift will go twice as far toward PPMD’s Gene Therapy Initiative.