Blog

September 29, 2021

WATCH: Connect with the Experts – Cardiac Care

Watch: Connect with the Experts – Cardiac Care Last week PPMD’s Rachel Schrader moderated a webinar with expert cardiologists to discuss important topics related to cardiac medications, imaging, and advanced cardiac care. PPMD recognizes families…

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WATCH: SRP-9001 Micro-Dystrophin Gene Therapy Clinical Update (Webinar Recording)

WATCH: SRP-9001 Micro-Dystrophin Gene Therapy Clinical Update Parent Project Muscular Dystrophy was joined by Sarepta Therapeutics for a webinar update on June 2, 2021. Sarepta was invited to present recent updates from their ongoing clinical…

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WATCH: Connect with the Experts – Navigating the College Campus with Duchenne

PPMD’s Rachel Schrader and Mena Scavina recently moderated a fantastic Connect with the Experts: Navigating the College Campus with Duchenne webinar. They led a dynamic conversation around what the college experience may look like for…

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WATCH: ASP0367 Development Program Update (Webinar Recording)

Astellas Pharma joined PPMD for a webinar on May 19, 2021 to provide an update on the company’s ASP0367 development program. If you missed the live event, the recording can be found below. …

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WATCH: Viltepso – A Treatment Option for Patients Amenable to Exon 53 Skipping (Webinar Recording)

NS Pharma joined PPMD for a webinar on April 22, 2021 to provide an update about VILTEPSO™, a treatment of Duchenne in patients who have a confirmed mutation of the DMD gene that is amenable to…

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Webinar Q&A: Gene Therapy – Turning Obstacles into Possibilities

Last week, PPMD held a webinar to discuss the lessons learned in Gene Therapy, current challenges for our community, and what the future holds for these promising treatments. After opening with an insightful presentation from…

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WATCH: Gene Therapy – Turning Obstacles into Possibilities (Webinar Recording)

On April 20, 2021, PPMD’s Pat Furlong & Eric Camino were joined by Drs. Nagaraju and Shieh for an interactive panel discussion on the lessons learned in Gene Therapy, current challenges for our community, and…

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WATCH: Transforming the Treatment Paradigm with Dyne Therapeutics (Webinar Recording)

Dyne Therapeutics joined Parent Project Muscular Dystrophy (PPMD) for a webinar on March 31, 2021 to provide an overview of the company’s mission, its novel FORCE platform designed to revolutionize drug delivery to muscle, and…

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WATCH: Santhera Pharmaceuticals Duchenne Drug Development Update (Webinar Recording)

Santhera Pharmaceuticals joined Parent Project Muscular Dystrophy (PPMD) for a webinar on March 24, 2021 to provide an update to the community about the investigational therapy vamorolone, the use of steroids to treat Duchenne muscular…

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WATCH: Solid Biosciences Presents Safety & Efficacy Update (Webinar Recording)

On March 16, 2021, Solid Biosciences joined PPMD for a webinar to provide a safety and efficacy update on the ongoing IGNITE DMD phase I/II clinical study of SGT-001 microdystrophin gene therapy in patients with…

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