August 22, 2022

WATCH: Dyne Therapeutics Update on DYNE-251 (Webinar Recording)

Dyne Therapeutics joined PPMD for a community webinar on Wednesday, July 20, 2022. Dyne provided an update on the recent U.S. Food and Drug Administration (FDA) announcement lifting the DYNE-251 clinical hold and clearing the…

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August 5, 2022

WATCH: Connect with the Experts – Pain Management (August 2022)

Many people with Duchenne experience pain every day that is often left untreated, or undertreated. Understanding the types of pain, what medications can be safely given, alternative measures of pain relief, and how to discuss…

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April 20, 2022

WATCH: Twice Weekly Steroids & Exercise for Duchenne – Study Update & Preliminary Findings (Webinar Recording)

Dr. Tanja Taivassalo joined PPMD for a community webinar last week to present an update on the University of Florida’s Department of Defense funded clinical trial evaluating the potential of low-dose twice weekly steroids and…

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April 11, 2022

Calling All Men With Becker – This Imaging Study is for You! (Webinar Recording & Resources)

PPMD was happy to recently host Dr. Krista Vandenborne, Director of ImagingNMD, and Dr. Claudia Senesac, ImagingNMD project manager, from University of Florida’s ongoing ImagingNMD program for a webinar on the development of a new…

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March 30, 2022

WATCH: Carrier Cardiac Care (Webinar Recording)

PPMD hosted a webinar on March 22, 2022 to discuss cardiac care for female carriers of Duchenne and Becker. Panelists discussed the importance of carrier health, learnings from the PPMD-sponsored carrier study at Nationwide Children’s…

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February 4, 2022

WATCH: FibroGen DMD Pamrevlumab Phase 3 Clinical Studies Highlight (Webinar Recording)

FibroGen joined PPMD for a webinar on February 2, 2022. During the webinar, FibroGen discussed the clinical rationale for the use of Pamrevlumab by highlighting its Phase 2 study in non-ambulatory participants with Duchenne and…

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November 18, 2021

WATCH: Connect with the Experts – Pulmonary Care (October 2021)

During this year’s PPMD Virtual Annual Conference, we hosted a panel titled: A Patient’s Take on Pulmonary Management. We received a large volume of questions during this live session, so many that we were only…

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November 9, 2021

WATCH: Pediatric COVID-19 Vaccination (ages 5-11) & Duchenne (Webinar Recording)

On November 5, 2021, PPMD invited Drs. Tim Cripe and Tim Franson back for another COVID-19 vaccine webinar to provide updates on the new pediatric approval and what it means for the Duchenne community. Our…

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October 18, 2021

WATCH: SRP-9001 Micro-Dystrophin Gene Therapy Clinical Update (Webinar Recording)

Last week, Parent Project Muscular Dystrophy was joined by Sarepta Therapeutics for a webinar to discuss the details of the EMBARK clinical trial (SRP-9001-301). If you missed the live event, the recording can be found below.*…

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September 29, 2021

WATCH: Connect with the Experts – Cardiac Care

Watch: Connect with the Experts – Cardiac Care Last week PPMD’s Rachel Schrader moderated a webinar with expert cardiologists to discuss important topics related to cardiac medications, imaging, and advanced cardiac care. PPMD recognizes families…

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