January 25, 2019

WATCH: Translarna® (ataluren) Development Update – Webinar Recording

On January 16, 2019, PTC Therapeutics joined Parent Project Muscular Dystrophy for a webinar update to provide the community with an overview of the Translarna development program with a focus on clinical trials that are…

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December 12, 2018

WATCH: The Heart of PPMD’s Research – Webinar Recording

ICYMI: Yesterday, I had the privilege of hosting an in depth look at PPMD’s cardiac research priorities in Duchenne for 2019. If you were unable to join us live, I hope you will take a…

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November 18, 2018

WATCH: Engaging Families in Care Guideline Development – Webinar Recording

On Wednesday, November 14, PPMD hosted a webinar on patient-centeredness of recently published endocrine care guidelines for Duchenne. Researchers from RAND Health Care and PPMD shared the results of their project that developed a new online…

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November 15, 2018

WATCH: PolarisDMD – Phase 3 Clinical Trial of Edasalonexent – Webinar Recording

PPMD and Catabasis as hosted a webinar on Wednesday, November 7 to discuss the Phase 3 PolarisDMD clinical trial studying edasalonexent in Duchenne muscular dystrophy, which is enrolling boys ages 4 to 7 (up to…

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October 31, 2018

WATCH: An Update on Corticosteroids – Webinar Recording

PPMD and Dr. John Brandsema hosted a webinar on October 24, 2018 to discuss the current guidelines for steroid use in Duchenne muscular dystrophy, emerging data, and best practices. If you missed the live event,…

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October 15, 2018

WATCH: Is Myostatin Still a Potential Therapeutic Target? – Webinar Recording

Myostatin is a negative regulator of muscle growth – a protein that stops muscle building and doesn’t let them get too big, as part of the natural regeneration process. In other words, if we can…

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October 3, 2018

WATCH: Puberty and Duchenne – Webinar Recording with Dr. Robert Benjamin, Pediatric Endocrinologist

Adolescence is a time of change – changing bodies, changing emotions, changing friends, changing lives. All of these changes are part of puberty, caused by increased levels of testosterone (the male sex hormone). But for…

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July 24, 2018

WATCH: HOPE-2 Duchenne Clinical Trial – Webinar Recording with Capricor

Capricor Therapeutics recently joined PPMD for a community webinar update to discuss the HOPE-2 trial. During the webinar, Capricor provided a background of CAP-1002 and its clinical development to date that has led to the…

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May 31, 2018

WATCH: Introducing PPMO – Webinar Recording with Sarepta Therapeutics

Sarepta Therapeutics, Inc. recently joined Parent Project Muscular Dystrophy (PPMD) for a community webinar update to discuss PPMO, Sarepta’s next generation precision RNA-targeting therapeutic platform for use in Duchenne muscular dystrophy. During the webinar, Sarepta…

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May 24, 2018

WATCH: Anti-Myostatin Adnectin RG6206 in Duchenne – Webinar Recording with Roche/Genentech

Roche/Genentech recently joined Parent Project Muscular Dystrophy for a webinar to provide an update on their Anti-Myostatin Adnectin (RG6206) development program. The team at Roche and its US affiliate, Genentech, and provided an overview of…

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