December 19, 2018

PPMD Awards $329,000 Grant to Binghamton University to Examine Role of Immune System on Dystrophin Restoration

PPMD is excited to award Dr. Kanneboyina Nagaraju and his team at Binghamton University’s School of Pharmacy and Pharmaceutical Sciences a $329,000 grant to continue his work examining the immune response to the production of…

Learn More

December 18, 2018

Keep hearts strong — all gifts doubled!

If you’re part of the Duchenne community, you have likely seen parents share updates from their child’s cardiac appointment. The anxiety of these appointments can be incredible — stability at a doctor’s appointment when you…

Learn More

December 13, 2018

ICER Announces the Review of Duchenne Products – What Does This Mean?

Thanks to decades of advocacy, funding and innovation, our healthcare landscape is rapidly changing. As new therapies emerge into the marketplace, patients, providers, and payers are faced with challenges as to how to discern which…

Learn More

December 13, 2018

PPMD Announces Partnership with THREAD to Enhance Current Duchenne Registry Platform

PPMD is excited to announce our new partnership with THREAD — a company specializing in remote/virtual patient research via their platform — to enhance the patient engagement and care management tools for The Duchenne Registry. Building…

Learn More

December 12, 2018

PPMD Hosts Inflammation Meeting

Steroids. If you are part of this community, you probably have strong feelings about steroids in Duchenne – feelings that can vary in range on any given day. But steroids are standard of care according…

Learn More

December 12, 2018

WATCH: The Heart of PPMD’s Research – Webinar Recording

ICYMI: Yesterday, I had the privilege of hosting an in depth look at PPMD’s cardiac research priorities in Duchenne for 2019. If you were unable to join us live, I hope you will take a…

Learn More

December 10, 2018

Your gift to critical cardiac research will be matched!

When PPMD started in 1994, research to treat Duchenne muscular dystrophy was virtually nonexistent. Nearly 25 years later, we have a clinical trial pipeline full of possibility with over 25 active trials, 30+ companies, and…

Learn More

December 6, 2018

Why the Heart Matters

Disclaimer: I am a selfish person. My sons Chris and Patrick died of heart failure. I agree the primary insult was pneumonia, but their hearts were broken in so many ways that they could not…

Learn More

November 30, 2018

Support heart health–all gifts matched!

For the last two years, you have helped support PPMD’s Gene Therapy Initiative and because of your support, we are seeing real results, real potential, real hope. But with all the progress we have made…

Learn More

November 29, 2018

An Update on Clinical Trial Innovation for Duchenne – a Master Protocol

PPMD is committed to making research and development of new medicines for families living with Duchenne as fast and efficient as possible.  Over the years, by listening to you, we have developed a clinical trials…

Learn More