Blog

PPMD to Host Duchenne Platform Trial Community Meeting & Live Stream

Please join PPMD and the Duchenne community at an open meeting on September 9, 2019 to provide input into the protocol design for the Duchenne Platform Trial, with the aim to increase access to therapeutic…

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PPMD Announces Children’s Hospital of Richmond at VCU as 26th Certified Duchenne Care Center

Today Parent Project Muscular Dystrophy (PPMD) named Children’s Hospital of Richmond at VCU (CHoR) the 26th Certified Duchenne Care Center (CDCC). This expanding certification program of elite centers, created in 2014 as part of PPMD’s…

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ICER Roundtable – What Does It Mean?

In December 2018, the Institute for Clinical and Economic Review (ICER) announced that it would be conducting an assessment of three Duchenne products over the next seven months. The ICER assessment is culminating in a…

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2019 #PPMDConference Presentations

2019 PPMD Annual Conference Resources & Recordings JUNE 27 – JUNE 29, 2019 | Orlando, Florida Thank you doesn’t begin to express our gratitude to everyone who participated in our 25th Annual Conference in Orlando,…

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PPMD: Your Strength, Your Family

PPMD: Your Strength, Your Family I had no intention of being part of the Duchenne community this long. When we started PPMD in 1994, I naively thought we would have a cure and I would…

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PPMD Awards $175,000 Grant to UCLA to Explore Optimization of CRISPR Technology in Duchenne

Parent Project Muscular Dystrophy (PPMD) is excited to announce that Drs. Melissa Spencer and April Pyle from the David Geffen School of Medicine at UCLA and the Center for Duchenne Muscular Dystrophy at University of…

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Jerry Mendell, MD named inaugural recipient of the Allen Distinguished Scholar in Pediatric Research

Nationwide Children’s Hospital has announced the inaugural recipient of the Allen Distinguished Scholar in Pediatric Research, Jerry Mendell, MD. Congratulations to Dr. Mendell on this incredibly deserved recognition! Thank you for your ongoing work in…

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PPMD Hosts Duchenne Clinical Outcomes Workshop

PPMD has been working for many years to engage critical policy makers and stakeholders within the regulatory and access environments. While we have learned a great deal over the past two years as we have…

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PPMD Awards $100,000 Grant to UCLA to Map the Immune Phenotype in Duchenne Muscular Dystrophy

PPMD is excited to announce that Dr. Carrie Miceli from the Center for Duchenne Muscular Dystrophy at University of California – Los Angeles (UCLA) is the recipient of a $100,000 grant to continue her work to…

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Your Duchenne Registry Data: Researchers Analyze Steroid Use

We have exciting news to share from The Duchenne Registry. A study using the Registry data was published this week in a well-known international journal, BMC Neurology. This study was led by researchers at Catabasis…

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