March 5, 2021

WATCH: Federally Funded Research Studies in Duchenne (Webinar Recordings)

Every year our community heads to Washington, D.C. as part of PPMD’s Advocacy Conference (this year, being held virtually on March 10th — and there’s still time to register!) to communicate to Congress the need for continued…

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March 3, 2021

PPMD Awards University of Florida Wellstone Center $348,891 Grant for Duchenne Gene Therapy Research

PPMD is pleased to award the University of Florida (UF) Wellstone Muscular Dystrophy Cooperative Center a grant for $348,891. The project titled “Understanding and Improving AAV Gene Therapy for DMD” is led by H. Lee…

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February 17, 2021

Duchenne UK and PPMD Award $350,000 to Address Immunological Challenges of Gene Therapy in Duchenne

Parent Project Muscular Dystrophy (PPMD) and Duchenne UK are excited to announce Professor Kanneboyina Nagaraju at Binghamton, the State University of New York, as the recipient of our Joint Research Grant Call of 2020. The…

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February 16, 2021

Save the Date for PPMD’s Annual Conference: Virtual Edition – June 23-26, 2021

PPMD’s Annual Conference – Virtual Edition June 23-26, 2021 It’s hard to believe that we are still in this pandemic. We are getting closer to safer days ahead and we want our Duchenne and Becker…

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February 10, 2021

“See you on the Road”: PPMD’s End Duchenne Tour 2021 Stops

Stemming from our PPMD’s Connect Roundtables, PPMD’s End Duchenne Tour stops were formally established in 2015 as the Every Single One Tour. Tour stops are typically one-day long events, providing updates on the latest clinical…

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February 10, 2021

Gene Therapy and Immune Response: Understanding Challenges and Strategies

PPMD recently announced the formation of the Pediatric Gene Therapy and Medical Ethics (PGTME) Working Group to address the challenges involved in gene therapy. As part of their recent educational series, the PGTME held a…

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February 9, 2021

PPMD Receives $100,000 Award from Duchenne Research Fund to Address Neurobehavioral Issues in Duchenne

Parent Project Muscular Dystrophy (PPMD) is excited to announce sponsorship from the Duchenne Research Fund for an award totaling over $100,000. As part of PPMD’s new Brain Initiative, the award will support work in understanding…

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January 21, 2021

WATCH: PGTME Hosts Gene Therapy Lecture Series

As the Duchenne community enters the era of gene therapy, many new concepts, terms and issues arise, including those related to research design, patient autonomy, sibling and family involvement, fairness in access and the quality…

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January 19, 2021

PPMD Invests $1 Million in Satellos Bioscience to Support New Regenerative Medicine Technology

Parent Project Muscular Dystrophy is excited to announce a $1 million programmatic investment in Satellos Bioscience Inc. (Satellos) to support the development of a new regenerative medicine for the therapeutic treatment of Duchenne. Duchenne is…

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January 12, 2021

WATCH: PGTME Hosts Gene Therapy Lecture Series

As the Duchenne community enters the era of gene therapy, many new concepts, terms and issues arise, including those related to research design, patient autonomy, sibling and family involvement, fairness in access and the quality…

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