January 4, 2022

Thank YOU for Joining the Power of Us!

I am grateful for your generosity this year and excited to announce that we have reached our goal of providing supplemental funding to the Wellstone Muscular Dystrophy Cooperative Research Centers. The Power of Us is…

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December 30, 2021

Tomorrow is the last chance to double your gift

I can’t believe it’s almost the beginning of a new year. In about a week, I will lace up my sneakers once again and join my chosen family for another Walt Disney World Marathon Weekend….

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December 26, 2021

Double the Impact of Your Gift Today!

Once Duchenne enters your life, you learn to be resilient even if it is against your wishes. You learn to come together to get through the tough times, even if it is with a community…

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December 17, 2021

Gene Editing Therapy Start-up Secures $3.4 Million Grant for Duchenne Research

MyoGene Bio has received a $3.4 million grant from the California Institute of Regenerative Medicine to advance its pre-clinical gene-editing studies in Duchenne, thanks to support from Parent Project Muscular Dystrophy (PPMD), Duchenne UK, and…

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December 15, 2021

Help PPMD raise $400,000 to invest in the future of Duchenne research

I am humbled to be working in Duchenne research, where patients and families have been the relentless driving force behind the progress we’ve made so far. We have seen the Power of Us realized, as…

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December 15, 2021

Second Chance — Win a NEW Nintendo Switch OLED!

THANK YOU, Duchenne Registry participants! As you might have heard, The Duchenne Registry was thrilled to recently give away a Nintendo Switch OLED to a Duchenne Registry participant who completed all of their surveys. The…

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December 7, 2021

Join the Power of Us with your gift today

Preparing to begin a new year, I always become a little nostalgic. I think about the year ahead of me and about the many years that have passed. This year, I can’t help but think…

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December 6, 2021

PPMD’s Drug Development Roundtable Meets to Explore Utilization of External Controls to Accelerate Research

At the heart of PPMD’s mission to end Duchenne lies our unwavering commitment to accelerate research. As part of our comprehensive research strategy, this includes a focus on enhancing the drug development process to ensure…

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December 3, 2021

Updating the Community-led Duchenne Guidance for FDA – The Power of Us!

The update to the Community-led Duchenne Guidance for FDA is well underway and on track to be submitted to the agency in the beginning of 2022. As you know, in 2014, we came together as…

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November 17, 2021

Win a NEW Nintendo Switch OLED!

For all of you gamers and parents of gamers, The Duchenne Registry is excited to announce we will be giving away a brand new, very hard to find, very fun to play Nintendo Switch OLED…

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