by: Parent Project Muscular DystrophyPPMD was joined by Drs. Russ Butterfield of University of Utah and Sue Apkon of Colorado Children’s to talk through some of the common questions around the recent FDA accelerated approval of ELEVIDYS. Drs. Butterfield and Apkon provided an overview of how gene therapy works, eligibility criteria listed in the ELEVIDYS label, risks and benefits, as well as logistics for accessing therapy safely.
