The Complexities of Duchenne (PPMD 2019 Conference) AGENDA 1:40-3:15p – The Complexities of Duchenne Moderator: Pat Furlong 1:40 – Duchenne: A Multisystem Disease – Stan Nelson, MD, PhD 2:00 – Variability: Modifiers to the Gene – Kevin Flanigan, MD 2:20 – Measuring Outcomes in the Face of Variability – Cliff Bechtold 2:40 – Challenges in Designing Trials – Craig McDonald, MD 3:00 – Q&A 2019 PPMD Annual Conference,Conferences & Meetings 5 years ago You may also like 11:23 Antisense Therapeutics 4 years ago Conferences & Meetings,In the Pipeline: Reducing Inflammation 13:19 PTC Therapeutics 4 years ago Approved Therapies,Conferences & Meetings 15:43 Sarepta Therapeutics 4 years ago Approved Therapies,Conferences & Meetings 7:48 What is a Post Market Study? 4 years ago Approved Therapies,Conferences & Meetings 35:48 DPT Meeting: Welcome & Introduction 5 years ago 2019 Duchenne Platform Trial Stakeholder Meeting,Conferences & Meetings 38:43 DPT Meeting: FDA Opening Remarks 5 years ago 2019 Duchenne Platform Trial Stakeholder Meeting,Conferences & Meetings 23:02 DPT Meeting: DPT Protocol in Practice 5 years ago 2019 Duchenne Platform Trial Stakeholder Meeting,Conferences & Meetings 43:44 DPT Meeting: Overview of DPT Proposed Protocol 5 years ago 2019 Duchenne Platform Trial Stakeholder Meeting,Conferences & Meetings «1…202122232425»Page 22 of 25