Research Row: Exon-Skipping Strategies
- Sarepta Therapeutics ( SRP-5051)
- Dyne Therapeutics (DYNE-251)
- PepGen (EDO51)
- BioMarin Pharmaceutical (BMN351)
- Wave Life Sciences (WVE-N531)
- Entrada Therapeutics (ENTR-601-44)
- Avidity Biosciences (AOC 1044)
- NS Pharma (NS-089)