January 6, 2025 /

Pat Chats: Dr. Sam Mackenzie talks about the Dystrophinopathy Clinical Research Network

Dr. Sam Mackenzie, pediatric neurologist at the University of Rochester Medical Center, joins Pat to chat about the development of PPMD’s Dystrophinopathy Clinical Research Network (DCRN). “We’re at a point where we really need to raise the bar on our evidentiary standard for what works well and what works best in combination, and reimagine the standards of care for this disease.” —Dr. Mackenzie Together, let’s advance the research evolution.


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