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November 13, 2018 /

Gene Therapy & Duchenne Muscular Dystrophy

Parent Project Muscular Dystrophy by: Parent Project Muscular Dystrophy

Gene therapy for Duchenne muscular dystrophy is centered on the goal of successfully introducing a smaller, but efficient version of dystrophin into the muscle cell. In early 2017 PPMD launched our Gene Therapy Initiative, a long-term concept that seeks to accelerate the potential of gene therapy as a therapeutic for Duchenne. Learn more about PPMD’s Gene Therapy Initiative.

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