Gene Therapy Approaches to Replace or Restore Dystrophin PF-06939926 – Kasia Lobello, MD (Pfizer, Inc.) RGX-202 – Jahannaz Dastgir, DO (REGENXBIO) scAAV9.U7-ACCA – Kevin Flanigan, MD (Nationwide Children’s Hospital) SGT-001 – Carl Morris, PhD (Solid Biosciences) SRP-9001 – Teji Singh, MD (Sarepta Therapeutics) 2022 PPMD Annual Conference,Conferences & Meetings 2 years ago You may also like 14:12 Closing Address: Looking Ahead to 2021 4 years ago 2020 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 26:14 Imaging DMD 4 years ago Conferences & Meetings,Resources & Tools 45:00 Gene Therapy: Q&A 4 years ago Conferences & Meetings,In the Pipeline: Gene Therapy gene therapy 44:59 CINRG Expanded Duchenne Natural History Study (eDNHS) 4 years ago Conferences & Meetings,Foundations of Drug Development 37:11 Genetics & The Duchenne Registry 4 years ago Beginning the Duchenne Journey,Conferences & Meetings 24:30 Research & Clinical Trials 4 years ago Beginning the Duchenne Journey,Conferences & Meetings 4:10 PPMD Community: Getting Involved 4 years ago Beginning the Duchenne Journey,Conferences & Meetings 22:23 Advocacy & Community Engagement 4 years ago Beginning the Duchenne Journey,Conferences & Meetings «1…1516171819…25»Page 17 of 25