Gene Correction (PPMD 2019 Conference)
0:00 – Gene Correction
Moderator: Richard Klein
1:16 – PTC – Richard Able Jr., PhD
20:30 – Sarepta – Gilmore O’Neill, M.B., M.M.SC.
38:57 – Wave – Michael Panzara, MD, MPH
59:13 – NS Pharma – Leslie Magnus, MD
1:10:36 – Q&A
1:23:36 – POLLING QUESTIONS