A Closer Look at the Potential of CRISPR/Cas9 in Duchenne (December 2016)

On December 15, 2016, PPMD hosted a webinar with Dr. Eric Olson from the Department of Molecular Biology at UT Southwestern Medical Center to review the basics of gene editing and next steps in the research and development potential of CRISPR/Cas9 in Duchenne. As you know, this holiday season PPMD is raising money to further explore the potential of gene editing technology like CRISPR/Cas9. But as with any new technology there are still many complex questions that must be answered as best we can, before it is ready to be tested in humans. This webinar reviewed the CRISPR technology and discussed two areas Dr. Olson and his team will first explore – how to test the efficacy and safety of dystrophins produced through this method.