ACT DMD Update with PTC (February 2014) On February 5, 2014, Dr. Robert Spiegel, Chief Medical Officer at PTC Therapeutics, presented an update about PTC’s Phase 3 study of ataluren, now known as the Ataluren Confirmatory Trial in DMD (ACT DMD). Research & Clinical Trial Webinars,Webinars 11 years ago You may also like 1:20:43 Webinar: Sarepta Therapeutics – Duchenne Gene Therapy Update 18 hours ago Research & Clinical Trial Webinars,Webinars elevidys,gene therapy,sarepta 29:52 Webinar: Duchenne Newborn Screening – Next Steps Following ACHDNC Dissolution 1 week ago Webinars newborn screening 59:32 Webinar: Wave Life Sciences – Update on FORWARD-53 Study of WVE-N531 3 weeks ago Research & Clinical Trial Webinars,Webinars wave life sciences,WVE-N531 1:00:09 Webinar: Avidity Biosciences – Topline Data from EXPLORE44® Clinical Trial 4 weeks ago Research & Clinical Trial Webinars,Webinars AOC 1044,avidity biosciences,del-zota 47:43 Webinar: Capricor Therapeutics – Update on Deramiocel for Cardiomyopathy in Patients with Duchenne 1 month ago Research & Clinical Trial Webinars,Webinars cap-1002,capricor,cardiac,deramiocel 02:15:11 PPMD’s Duchenne Early Intervention Symposium 2 months ago Webinars newborn screening 01:08:05 Webinar: Solid Biosciences – Update on Gene Therapy Candidate SGT-003 2 months ago Research & Clinical Trial Webinars,Webinars gene therapy,sgt-003,solid biosciences 58:14 Webinar: Sevasemten – CANYON Trial Topline Results 4 months ago Research & Clinical Trial Webinars,Webinars edg-5506,edgewise 123…26»Page 1 of 26