When PPMD started in 1994, research to treat Duchenne muscular dystrophy was virtually nonexistent. Nearly 25 years later, we have a clinical trial pipeline full of possibility with over 25 active trials, 30+ companies, and support at the federal, state, and local level. PPMD, thanks to your donations, has invested in nearly every therapeutic approach being explored. We have supported cardiac research and care, because the heart is a muscle too.

Progress is being made. Slower than any of us would like, but it is happening. Donate today and your gift will help speed up this process, helping us invest in promising cardiac research, getting to the heart of Duchenne. Plus, all donations will be doubled until we reach our goal of $550,000!

The more questions we answer, the more questions there are to ask — questions PPMD is exploring by supporting the work of cutting edge research. Your donation today is generously being matched by a family who understands how critical heart health is in Duchenne and will help us support projects that:

• Study the effects of current gene therapy on the heart to better understand the effect it is having on the cardiac system
• Explore potential gene therapy technology that could directly affect heart health, since most therapies focus on skeletal muscle rescue
• Understand cardiac MRIs and how we can use that knowledge to better characterize and ultimately prevent dystrophin cardiomyopathy
• Continue to focus on the cardiac health of carrier moms, so that everyone in a family affected by Duchenne is cared for and treated

Science is about finding answers. That is why we have continued to expand our Cardiac Initiative — a program that to date has invested $5 million into cardiac research and care in Duchenne. Today we are at a critical point and we need your help to further expand our robust exploration and investment into research.

I am proud to lead PPMD’s research strategy and I am inspired by the breadth of projects and the number of scientists dedicated to the fight to end Duchenne. At PPMD, we are looking at the entire individual and insisting we understand how each and every potential treatment could affect each and every system of our children. And at the heart of everything is…the heart.

Since starting with PPMD in 2016, I have seen firsthand the hope and optimism that thrives in this community. That determination and passion, combined with thorough research and comprehensive care, will alter the progression of this devastating disease.

Donate today to help PPMD continue to fund the science that will help us save hearts and end Duchenne. Your gift will be doubled until we reach our goal of $550,000.

Sincerely,

Abby Bronson
PPMD’s SVP of Research Strategy

P.S. Now is the time to push forward our robust cardiac research agenda. With your help, we can help heal the heart. Your donation today will help build the pathway for tomorrow. Have your donation doubled to advance this critical cardiac research.