SRD-001 is an adeno-associated virus (AAV) mediated gene transfer that contains an engineered version of the SERCA2a gene. This AAV1 mediated delivery of the SERCA2a transgene to the heart may help regulate calcium balance in the cardiac muscle.
A Phase 1 study is not yet recruiting.
This program is sponsored by Sardocor Corp.
NOT YET RECRUITING | Modulation of SERCA2a of Intra-Myocytic Calcium Trafficking in Cardiomyopathy Secondary to Duchenne Muscular Dystrophy (MUSIC-DMD) |